A revolution in medicine is underway as researchers advance a growing number of promising investigational gene therapies, including many for rare diseases.
Following decades of research, the concept of “genes as medicine” is becoming a reality. Last year, 802 clinical trials of gene and cellular therapies were underway worldwide, including 66 Phase 3 trials, according to the Alliance for Regenerative Medicine.
Are we ready for the revolution? Research conducted by SmithSolve and partners reveals significant and persistent knowledge gaps about gene therapy across diverse stakeholders. A unified approach to communication and education will be critical to support informed decision-making and patient access to these therapies.
To learn more …
- Read the news release here.
- For additional commentary about the gene therapy revolution from two of the co-authors of this paper, Chris Smith and Patti Engel, read the Rare Collective™ blog post: “Ready for a Revolution: Improving Understanding of Gene Therapy.”
Download the Poster
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